PTC Therapeutics’ gene therapy, Kebilidi to treat AADC deficiency receives US FDA approval: Warren, New Jersey Friday, November 15, 2024, 10:00 Hrs [IST] PTC Therapeutics, Inc., ...
I just felt nervous at the thought of having to deal with a feeding tube or something. I was living in a two-bedroom condo ... James’s pediatrician agreed that James wasn’t hitting his milestones and ...
First-ever FDA approval for gene therapy directly administered to the brain - - Priority review voucher granted - - Broad label including children and adults - - ...
WARREN, NJ, USA I November 13, 2024 I PTC Therapeutics, Inc. (NASDAQ: PTCT) announced today the U.S. Food and Drug Administration (FDA) accelerated approval of its gene therapy for the treatment of ...
Modifying Treatment for AADC Deficiency in the United States SOLANA BEACH, CA / / November 13, 2024 / ClearPoint Neuro, Inc. (Nasdaq:CLPT) (the 'Company'), a global therapy-enabling platform company ...